Description
Kalydeco is a medicine for the treatment of cystic fibrosis (CF) patients. This medicine is only for CF patients with a specific genetic mutation on the CFTR gene: G551D, G1244E, G1349R G178R, G551S, S1251N, S1255P, S549N or S549R.
On 26/11/2015, the manufacturer of Kalydeco, Vertex Pharmaceuticals, and the NIHDI signed an agreement for the temporary reimbursement of Kalydeco. As part of this temporary reimbursement, additional data should be collected for all patients treated with Kalydeco. With this data, Vertex Pharmaceuticals must prepare reports that are intended for the NIHDI and that must allow to evaluate the effectiveness of the medicine based on the following questions: a) What is the (long-term) effect on disease progression, on the use of standard therapies, on the need for lung transplantation and on mortality?; b) What is the actual reduction in antibiotic use and hospitalizations?; c) What is the effect on improving survival?. Based on these reports, the NIHDI will decide whether the reimbursement can be continued.
Resources
| Name | Format | Description | Link |
|---|---|---|---|
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders CSV | CSV | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Data User JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| HD Data Collection Definition of project HDBP0068 KALYDECO v2.1 20190916 | xlsx | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Stakeholders JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 Legal JSON | JSON | Open resource | |
| b562f5a1-baa4-4581-92aa-5b5cdb3ab743 SCRA CSV | CSV | Open resource |
Tags
- age
- âge
- alliance-nationale-des-mutualités-chrétiennes-(anmc)
- artikel-81
- atc-l1-r
- atc-r07ax02
- belgië-(country)
- belgique-(country)
- belgium-(country)
- beveiligde-elektronische-brievenbus-(ehealthbox)
- boîte-aux-lettres-électronique-sécurisée-(ehealthbox)
- caisse-auxiliaire-d'assurance-maladie-invalidité-(caami)
- caisse-des-soins-de-santé-de-la-sncb-holding-(hr-railcare)
- cas-873054-44-5
- chebi-66901
- chembl-2010601
- chemspider-17347474
- civars
- cobrha-common-base-registry-for-healthcare-actor-(ehealth)
- codage,-anonymisation-et-ttp-(ehealth)
- codering,-anonimisering-en-ttp-(ehealth)
- collège-intermutualiste-national-(cin)
- comité-de-sécurité-de-l'information:-chambre-sécurité-sociale-et-santé
- cystic-fibrosis
- cystische-fibrose
- drugbank-db08820
- echa-100.226.211
- fibrose-kystique
- gender
- geneesmiddelen-hoofdstuk-iv
- geslacht
- hdbp0068
- healthdata.be-(sciensano)
- health-technology-assessment-procedure
- hôpital
- hospital
- hta
- hulpkas-voor-ziekte-en-invaliditeitsverzekering-(hziv)
- icd10-e00–e90
- identificatienummer-van-de-sociale-zekerheid-(insz)
- informatieveiligheidscomité:-kamer-sociale-zekerheid-en-gezondheid
- institut-national-d'assurance-maladie-invalidité-(inami)
- iuphar-4342
- ivacaftor
- kalydeco
- kas-der-geneeskundige-verzorging-van-de-nmbs-holding-(hr-railcare)
- kegg-d09916
- landesinstitut-für-kranken-und-invalidenversicherung-(likiv)
- landsbond-der-christelijke-mutualiteiten-(lcm)
- landsbond-van-de-neutrale-ziekenfondsen-(lnz)
- landsbond-van-de-onafhankelijke-ziekenfondsen-(mloz)
- landsbond-van-liberale-mutualiteiten-(llm)
- leeftijd
- managed-entry-agreement
- médicaments-chapitre-iv
- medlineplus-a612012
- mesh-c545203
- mesh-d003550
- mucoviscidose
- mucoviscidosis
- nationaal-intermutualistisch-college-(nic)
- nationaal-verbond-van-socialistische-mutualiteiten-(nvsm)
- national-institute-for-health-and-disability-insurance-(nihdi)
- nidhi-number
- numéro-de-registre-national-(nrn)
- numéro-d'identification-de-la-sécurité-sociale-(niss)
- numéro-inami
- project-completed
- pubchem-16220172
- rijksinstituut-voor-ziekte-en-invaliditeitsverzekering-(riziv)
- rijksregisternummer-(rrn)
- riziv-nummer
- sex
- sexe
- snomed-ct-110462006
- snomed-ct-190905008
- source-data-at-healthdata.be-(sciensano)
- unii-1y740ill1z
- union-nationale-des-mutualités-libérales-(unml)
- union-nationale-des-mutualités-libres-(unml)
- union-nationale-des-mutualités-neutres-(unmn)
- union-nationale-des-mutualités-socialistes-(solidaris-unms)
- vertex-pharmaceuticals-(company)
- vx-770
- ziekenhuis